Page 27 - Let them speak Towards a patient reported outcome measure set for
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Chapter 2
Navigating the outcome
maze: a scoping review of
outcomes and instruments
in clinical trials in genetic
neurodevelopmental disorders
and intellectual disability
Annelieke R. Müller, Nadia Y. van Silfhout, Bibiche den Hollander, Dick H.
C. Kampman, Lianne Bakkum, Marion M. M. G. Brands, Lotte Haverman,
Caroline B. Terwee, Carlo Schuengel, Joost Daams, David Hessl,
Frits A. Wijburg, Erik Boot, Agnies M. van Eeghen
Therapeutic Advances in Rare Disease. 2024, 5, 26330040241245721.
