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                                    Chapter 4Cannabidiol (Epidyolex®) for severe behavioral manifestations in patients with Tuberous Sclerosis Complex, mucopolysaccharidosis type III and Fragile X syndrome: protocol for a series of randomized, placebo-controlled N-of-1 trialsAnnelieke R. Müller*, Bibiche den Hollander*, Peter M. van de Ven, Kit C.B. Roes, Lisa Geertjens, Hilgo Bruining, Clara D.M. van Karnebeek, Floor E. Jansen, Marie-Claire Y. de Wit, Leontine W. ten Hoopen, André B. Rietman, Bram Dierckx, Frits A. Wijburg, Erik Boot, Marion M.M.G. Brands, Agnies M. van Eeghen* Both authors contributed equally.SubmittedAnnelieke Muller sHL.indd 77 14-11-2023 09:07
                                
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